SAN DIEGO — As its competitors celebrate the landmark approval of two sickle cell gene therapies, Editas Medicine detailed promising early results in a small group of patients for its own gene-edited sickle cell treatment.
Across two studies in sickle cell disease and transfusion-dependent β-thalassemia, Editas reported that 11 patients have not had pain crises known as vaso-occlusive events since receiving its gene-edited therapy, known as EDIT-301. But, on average, the patients have not been followed for very long in the study — between a few weeks and one and a half years. The data were presented at the American Society of Hematology annual meeting on Monday.
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