A newly developed “GPS nanoparticle” injected intravenously can home in on cancer cells to deliver a genetic punch to the protein implicated in tumor growth and spread, according to researchers from Penn State.
Freeline touts positive data for Gaucher disease therapy – Pharmaceutical Technology
Freeline’s gene therapy FLT201 introduces a transgene to produce an engineered GCase variant, the enzyme responsible for the symptoms of Gaucher disease. Credit: dizain via