In February, Norma Brambila’s teenage daughter wrote her a letter she now carries in her purse. It is a drawing of a rose, and a note encouraging Brambila to “keep fighting” her sickness and reminding her she’d someday join her family in heaven.
Only a small fraction of rare pediatric designations have led to vouchers, new FDA analysis shows
Out of hundreds of potential drugs with rare pediatric disease designations, only 7% of them have won priority review vouchers from the FDA, according to
February 29, 2024