A drug commonly used to treat cystic fibrosis improved outcomes for patients with severe COVID-19 pneumonia and could be used to treat other respiratory infections, according to clinical trial results from researchers at UCL, UCLH and the Francis Crick Institute.
Updated: FDA approves Sarepta’s Duchenne muscular dystrophy gene therapy via accelerated pathway
The FDA granted accelerated approval to Sarepta Therapeutics’ Duchenne muscular dystrophy gene therapy for boys aged 4 and 5 in a decision that allows access
June 23, 2023