Gene therapy could potentially cure genetic diseases but it remains a challenge to package and deliver new genes to specific cells safely and effectively. Existing methods of engineering one of the most commonly used gene-delivery vehicles, adeno-associated viruses (AAV), are often slow and inefficient.
Pfizer gene therapy gets hemophilia B approval in Canada, setting stage for CSL rivalry
Pfizer has secured an approval for its gene therapy for hemophilia B in Canada, months ahead of an expected decision in the US. The approval