Across two clinical trials, gene therapy restores hearing in children deaf since birth: #ASGCT24

BAL­TI­MORE — Ten out of 11 chil­dren who were born deaf can now hear af­ter re­ceiv­ing a gene ther­a­py from a Shang­hai biotech, ac­cord­ing to new re­sults shared Thurs­day.

The chil­dren who re­cov­ered their hear­ing are al­so show­ing im­prove­ments in their abil­i­ty to speak. Some are say­ing the words “ma­ma” and “ba­ba” — Chi­nese for “mom” and “dad” — for the first time, said Yi­lai Shu of Fu­dan Uni­ver­si­ty in Shang­hai, who led the ear­ly-stage clin­i­cal study.

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