A new study shows that delivery of gene therapy to correct the gene mutations that cause CLN2 disease, or Batten disease, directly into the cerebrospinal fluid (CSF) has potential therapeutic effects.
Columbia scientists reel as Trump administration cancels grants, hitting broad suite of research
NEW YORK — Uma Reddy was sitting at her kitchen table Monday night, wrapping up patient notes, when the notice finally came: The $16.6 million
March 12, 2025