Cells are the basic units of life — but when it comes to cells, if you think basic means simple, think again. Cells are complicated, with many millions of biochemical reactions per second seething within their confines. They also tend to be tiny, so it’s not easy to spy on their operations.
Potentially Protective Agent Shows Benefit in Niemann-Pick Type C
Patients with Niemann-Pick disease type C who received N-acetyl-L-leucine (NALL), an agent that potentially ameliorates lysosomal and metabolic dysfunction, showed reduced neurologic signs and symptoms
February 1, 2024