As a neurodegenerative disease characterized by childhood onset dementia, Sanfilippo syndrome causes immense suffering in many ways, including pain, loss of speech, extreme agitation, and distress, gastrointestinal symptoms, and profound sleep disturbance.
Pharmalittle: We’re reading about weight loss drugs, a cell therapy for melanoma, and more
Good morning, everyone, and welcome to another working week, which is getting off to a late start on this side of the pond thanks to