Primary sclerosing cholangitis (PSC) is a rare progressive liver disease that damages bile ducts and significantly increases the risk of bile duct cancer, particularly a type called cholangiocarcinoma (CCA).
As Sarepta execs talk up Duchenne confirmatory trial results, investors and analysts remain divided on how flexible FDA will be
Anyone listening to Sarepta’s call Monday after the biotech released trial data for its Duchenne muscular dystrophy gene therapy would have thought the company hit