A promising daily tablet is effective at increasing height and improving proportional limb growth in children with achondroplasia, the most common form of dwarfism, according to a new study.
Intellia’s gene editing therapy shows early potential in rare heart condition – Pharmaceutical Technology
Transthyretin amyloidosis with cardiomyopathy (ATTR-CM) presents with symptoms primarily related to heart failure and impaired cardiac function. Credit: Rawpixel.com via Shutterstock. Intellia Therapeutics has announced