Mental health courts can struggle to fulfill decades-old promise

Blue­bird bio re­port­ed that 17 peo­ple with sick­le cell dis­ease have start­ed the process of re­ceiv­ing its gene ther­a­py Lyf­ge­nia. Blue­bird said in its …

Ul­tragenyx took a step to­ward es­tab­lish­ing a po­ten­tial new sur­ro­gate bio­mark­er Tues­day morn­ing, pre­sent­ing da­ta for a rare dis­ease with no ap­proved treat­ments. Re­searchers are