Cerebral autosomal recessive arteriopathy with subcortical infarcts and leukoencephalopathy (CARASIL) is a rare, severe, and deadly genetic disorder characterized by damage to small blood vessels in the brain and which triggers strokes.
Taysha stops developing a gene therapy amid debate over FDA’s stance on ultra-rare trials
Taysha Gene Therapies discontinued development of a neurodegenerative therapy after the FDA again insisted on a potentially impossible study, the company said Tuesday. It’s yet
September 21, 2023