The Patient-Centered Outcomes Research Institute (PCORI) today announced funding awards totaling $208 million to support 17 new comparative clinical effectiveness research (CER) studies, including four trials of particularly large scale and scope tackling complex questions.
PTC finds itself in quagmire of regulatory setbacks, pushes back timeline on PKU treatment
PTC Therapeutics has delayed its plans by nine months to apply for FDA approval of its treatment for phenylketonuria, a rare disease that causes protein
October 28, 2023