Genetic changes or mutations can cause hereditary kidney disease, which can eventually lead to dialysis or the need for kidney transplantation. Identifying the cause of inherited kidney disease is the first step in identifying a treatment.
EMA CHMP endorses Mirum Pharmaceuticals’ LIVMARLI for PFIC
Mirum is seeking to expand its label for younger PFIC patients in 2024 in the US. Credit: Kmpzzz/Shutterstock.com. The European Medicines Agency’s Committee for Medicinal