Transgender people face challenges getting needed care

Ahead of an FDA advisory committee meeting on Thursday, agency reviewers cast doubt on the efficacy of elamipretide for Barth syndrome, an ultra-rare disease that

In­smed wants to rec­og­nize pa­tients who feel un­seen or ig­nored, pub­lish­ing a new sur­vey, host­ing a pan­el dis­cus­sion with celebri­ty par­tic­i­pants and de­but­ing a new